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Cardiometabolic
Includes cardiometabolic-related technologies including indications like NASH, Cirrhosis, CKD, nephrosis, and diabetic kidney disease.
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Al-Walid Mohsen
2 results
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Novel Treatment for Acidemias
06006
University of Pittsburgh researchers have developed a novel treatment for treating disease conditions that result from deficiency of succinyl-CoA including propionic acidemia and fatty acid disorders.
Al-Walid Mohsen
Therapeutic Modality
Small Molecule
Endocrinology
and
Metabolic
Diseases
Other
Pediatrics
Rare disease
2022-04-15
Novel Treatments for Mitochondrial Disorders
03999
Inborn errors of metabolism (IEMs) disrupt biochemical pathways through deficiency of a particular enzyme.
Al-Walid Mohsen
Therapeutic Modality
Drug Discovery - Target
Endocrinology
and
Metabolic
Diseases
Other
2016-07-29